Showing 13 to 24 of 42 results
Successful Gene Editing Treats Rare Genetic Disease in Baby
A baby with severe CPS1 deficiency, a rare genetic disorder affecting approximately one in a million infants, received a custom gene-editing therapy using CRISPR base editing, resulting in significant health improvements within months, opening possibilities for treating other rare genetic diseases.
Successful Gene Editing Treats Rare Genetic Disease in Baby
A baby with severe CPS1 deficiency, a rare genetic disorder affecting approximately one in a million infants, received a custom gene-editing therapy using CRISPR base editing, resulting in significant health improvements within months, opening possibilities for treating other rare genetic diseases.
Progress
40% Bias Score
Gene Editing Successfully Treats Baby's Life-Threatening Genetic Disorder
Doctors successfully used a personalized gene-editing therapy to treat baby KJ Muldoon's life-threatening genetic disorder, carbamoyl phosphate synthetase 1 (CPS1), showing potential for treating numerous rare diseases previously untreatable.
Gene Editing Successfully Treats Baby's Life-Threatening Genetic Disorder
Doctors successfully used a personalized gene-editing therapy to treat baby KJ Muldoon's life-threatening genetic disorder, carbamoyl phosphate synthetase 1 (CPS1), showing potential for treating numerous rare diseases previously untreatable.
Progress
40% Bias Score
Personalized Gene Editing Shows Promise in Treating Rare Metabolic Disorder
A US baby, KJ, diagnosed with the ultra-rare CPS1 deficiency, received a groundbreaking personalized gene-editing therapy using base editors, showing promising results and offering a new hope for treating such rare metabolic disorders. The treatment was delivered in two doses via lipid nanoparticles...
Personalized Gene Editing Shows Promise in Treating Rare Metabolic Disorder
A US baby, KJ, diagnosed with the ultra-rare CPS1 deficiency, received a groundbreaking personalized gene-editing therapy using base editors, showing promising results and offering a new hope for treating such rare metabolic disorders. The treatment was delivered in two doses via lipid nanoparticles...
Progress
40% Bias Score
Personalized Gene Therapy Shows Promise in Treating Baby with Rare Metabolic Disorder
In February 2025, a baby born with a life-threatening metabolic disorder received a personalized gene therapy in the US, showing significant health improvements and enabling the baby to return home, representing a potential breakthrough for treating rare genetic diseases with personalized base editi...
Personalized Gene Therapy Shows Promise in Treating Baby with Rare Metabolic Disorder
In February 2025, a baby born with a life-threatening metabolic disorder received a personalized gene therapy in the US, showing significant health improvements and enabling the baby to return home, representing a potential breakthrough for treating rare genetic diseases with personalized base editi...
Progress
40% Bias Score
Gene Editing Therapy Shows Promise in Treating Rare Genetic Disorder
Nine-month-old KJ Muldoon, diagnosed with severe CPS1 deficiency, a rare genetic disorder affecting one in a million babies, is thriving after receiving a custom CRISPR-based gene editing therapy developed in six months by researchers at Children's Hospital of Philadelphia and Penn Medicine.
Gene Editing Therapy Shows Promise in Treating Rare Genetic Disorder
Nine-month-old KJ Muldoon, diagnosed with severe CPS1 deficiency, a rare genetic disorder affecting one in a million babies, is thriving after receiving a custom CRISPR-based gene editing therapy developed in six months by researchers at Children's Hospital of Philadelphia and Penn Medicine.
Progress
40% Bias Score
CRISPR-Edited Microglia Show Promise in Reversing Alzheimer's in Mice
UCI scientists have developed a new Alzheimer's treatment using CRISPR gene-edited microglia immune cells to break down amyloid plaques in mice, reversing neurodegeneration; this targeted therapy may help overcome the blood-brain barrier, offering a promising new avenue for Alzheimer's and other neu...
CRISPR-Edited Microglia Show Promise in Reversing Alzheimer's in Mice
UCI scientists have developed a new Alzheimer's treatment using CRISPR gene-edited microglia immune cells to break down amyloid plaques in mice, reversing neurodegeneration; this targeted therapy may help overcome the blood-brain barrier, offering a promising new avenue for Alzheimer's and other neu...
Progress
48% Bias Score
Gene Editing Successfully Treats Rare Genetic Disease in Infant
A baby, K.J. Muldoon, born with severe CPS1 deficiency, a rare genetic disease affecting approximately one in a million infants, is thriving after receiving a custom CRISPR-based gene-editing therapy developed by the Children's Hospital of Philadelphia and Penn Medicine, offering hope for millions w...
Gene Editing Successfully Treats Rare Genetic Disease in Infant
A baby, K.J. Muldoon, born with severe CPS1 deficiency, a rare genetic disease affecting approximately one in a million infants, is thriving after receiving a custom CRISPR-based gene-editing therapy developed by the Children's Hospital of Philadelphia and Penn Medicine, offering hope for millions w...
Progress
48% Bias Score
Successful Gene Editing Treatment for Rare Genetic Disease
A 9.5-month-old baby, KJ Muldoon, successfully received a custom CRISPR-based gene editing therapy for severe CPS1 deficiency, a rare genetic disease affecting approximately one in a million babies. The treatment significantly improved his health, demonstrating the potential of personalized gene the...
Successful Gene Editing Treatment for Rare Genetic Disease
A 9.5-month-old baby, KJ Muldoon, successfully received a custom CRISPR-based gene editing therapy for severe CPS1 deficiency, a rare genetic disease affecting approximately one in a million babies. The treatment significantly improved his health, demonstrating the potential of personalized gene the...
Progress
40% Bias Score
Successful Gene Editing Therapy Treats Rare Genetic Disorder in Baby
A baby with CPS1 deficiency, a rare genetic disease affecting approximately one in a million infants, successfully underwent a custom gene-editing therapy using base editing, resulting in significant improvement in his health within months.
Successful Gene Editing Therapy Treats Rare Genetic Disorder in Baby
A baby with CPS1 deficiency, a rare genetic disease affecting approximately one in a million infants, successfully underwent a custom gene-editing therapy using base editing, resulting in significant improvement in his health within months.
Progress
40% Bias Score
Gene Editing Therapy Shows Promise for Rare Genetic Disorder
A nine-and-a-half-month-old baby in Pennsylvania with severe CPS1 deficiency, a rare genetic disorder affecting roughly one in a million infants, is thriving after receiving a custom-designed gene editing therapy using CRISPR base editing, offering hope for millions with rare genetic diseases.
Gene Editing Therapy Shows Promise for Rare Genetic Disorder
A nine-and-a-half-month-old baby in Pennsylvania with severe CPS1 deficiency, a rare genetic disorder affecting roughly one in a million infants, is thriving after receiving a custom-designed gene editing therapy using CRISPR base editing, offering hope for millions with rare genetic diseases.
Progress
32% Bias Score
1977 Twin Study Reveals Strong Genetic Link to Autism
A 1977 study on twins showed a strong genetic link to autism; identical twins had a 90% chance of both having autism if one did, while fraternal twins had a 34% chance. This shifted understanding from solely environmental factors to recognizing a significant genetic component, though the precise gen...
1977 Twin Study Reveals Strong Genetic Link to Autism
A 1977 study on twins showed a strong genetic link to autism; identical twins had a 90% chance of both having autism if one did, while fraternal twins had a 34% chance. This shifted understanding from solely environmental factors to recognizing a significant genetic component, though the precise gen...
Progress
48% Bias Score
Gene-Edited Wolves Mimic Dire Wolves: Implications for De-Extinction
Colossal Biosciences created three dire wolf puppies by genetically modifying gray wolves using ancient DNA, cloning, and CRISPR technology; this differs from true de-extinction, which requires complete original DNA recovery.
Gene-Edited Wolves Mimic Dire Wolves: Implications for De-Extinction
Colossal Biosciences created three dire wolf puppies by genetically modifying gray wolves using ancient DNA, cloning, and CRISPR technology; this differs from true de-extinction, which requires complete original DNA recovery.
Progress
16% Bias Score
Showing 13 to 24 of 42 results